Company Filing History:
3 out of 2,596 
1 out of 832,718 Years Active: 2023-2025
Title: Juliette Hordeaux: A Pioneer in Gene Therapy
Introduction
Juliette Hordeaux, based in Philadelphia, PA, has made significant contributions to the field of gene therapy with a focus on rare genetic disorders. As an inventor, she holds a remarkable portfolio of four patents that highlight her innovative work in developing treatments for debilitating conditions.
Latest Patents
Among her most notable inventions is a patent concerning compositions useful in the treatment of metachromatic leukodystrophy. This patent presents a recombinant adeno-associated virus (rAAV) featuring an AAVhu68 capsid, which encodes a functional human arylsulfatase A (ARSA). The invention includes a production system for generating the rAAV, alongside a pharmaceutical composition that can effectively treat individuals suffering from this condition or ameliorate its symptoms.
Another significant patent involves gene therapy for mucopolysaccharidosis IIIB (MPS IIIB). This innovative approach utilizes a recombinant AAV that contains an engineered nucleic acid sequence encoding a functional human N-acetyl-alpha-glucosaminidase (hNAGLU). The patent outlines a pharmaceutical composition that targets the treatment of patients diagnosed with MPS IIIB, which could markedly improve the quality of life for those affected by this rare disorder.
Career Highlights
Juliette has taken on pivotal roles within esteemed institutions, notably at the University of Pennsylvania, where her research and innovations have paved the way for advanced therapeutic strategies. Her work continues to impact the landscape of gene therapy, potentially making her a leading figure in modern biotechnology.
Collaborations
Throughout her career, Juliette has collaborated with notable professionals in the field, including James M. Wilson and Nathan Katz. These partnerships have undoubtedly enriched her research endeavors and fostered a productive environment for innovation and discovery.
Conclusion
Juliette Hordeaux exemplifies the spirit of innovation in the realm of gene therapy. Her patents represent not just personal achievements, but also a beacon of hope for patients suffering from rare genetic conditions. Through her groundbreaking work, she continues to inspire the medical and scientific communities.
Inventor’s Patent Attorneys refers to legal professionals with specialized expertise in representing inventors throughout the patent process. These attorneys assist inventors in navigating the complexities of patent law, including filing patent applications, conducting patent searches, and protecting intellectual property rights. They play a crucial role in helping inventors secure patents for their innovative creations.