The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
May. 23, 2017

Filed:

Oct. 16, 2014
Applicants:

Icahn School of Medicine AT Mount Sinai, New York, NY (US);

The Trustees of the University of Pennsylvania, Philadelphia, PA (US);

Inventors:

Silvia Muro Galindo, Silver Spring, MD (US);

Vladimir R. Muzykantov, Bryn Athyn, PA (US);

Edward Howard Schuchman, Haworth, NJ (US);

Attorney:
Primary Examiner:
Int. Cl.
CPC ...
A61K 9/127 (2006.01); A61K 39/00 (2006.01); A61K 38/46 (2006.01); C12N 9/16 (2006.01); C12N 9/14 (2006.01); C12P 19/34 (2006.01); C12P 21/06 (2006.01); C12N 15/00 (2006.01); C12N 5/00 (2006.01); C07H 21/04 (2006.01); A61K 47/48 (2006.01); C07K 16/28 (2006.01); A61K 38/00 (2006.01);
U.S. Cl.
CPC ...
A61K 38/465 (2013.01); A61K 47/48561 (2013.01); C07K 16/2821 (2013.01); C12N 9/16 (2013.01); A61K 38/00 (2013.01); C07K 2317/77 (2013.01); C07K 2319/035 (2013.01); C12Y 301/04012 (2013.01); Y10T 428/2982 (2015.01); Y10T 428/2991 (2015.01);
Abstract

The present invention relates to compositions and methods for delivering lysosomal proteins. The compositions and methods described herein permit the targeted delivery of exogenous lysosomal proteins to cell surface proteins that allow their internalization via non-clathrin pathways. The present invention further relates to the use of the compositions and methods for enzyme replacement therapy of lysosomal storage diseases. Nucleic acids, recombinant cells and kits useful for making and using the compositions of the invention are also provided.


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