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The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Patent No.:

US 9499818 B1

PDFFull Text
Date of Patent:
Nov. 22, 2016

Filed:

Feb. 25, 2015

Methods and means for efficient skipping of at least one of the exons 51-53, 55, 57 and 59 of the human duchenne muscular dystrophy gene

Applicants:

Academisch Ziekenhuis Leiden, Leiden, NL;

Prosena Technologies B.v., Leiden, NL;

Inventor:

Judith Christina Theodora van Deutekom, Dordrecht, NL;

Assignees:

BioMarin Technologies, B.V., Leiden, NL;

Academisch Ziekenhuis Leiden, Leiden, NL;

Attorney:

Sunstein Kann Murphy & Timbers LLP

Primary Examiner:

Dana Shin

Int. Cl.
CPC ...
C07H 21/04 (2006.01); C12N 15/113 (2010.01); A61K 31/56 (2006.01); A61K 31/57 (2006.01); A61K 38/17 (2006.01); A61K 45/06 (2006.01); A61K 48/00 (2006.01); A61K 31/7088 (2006.01);
U.S. Cl.
CPC ...
C12N 15/113 (2013.01); A61K 31/56 (2013.01); A61K 31/57 (2013.01); A61K 38/1719 (2013.01); A61K 45/06 (2013.01); A61K 31/7088 (2013.01); A61K 48/00 (2013.01); C12N 2310/11 (2013.01); C12N 2310/315 (2013.01); C12N 2310/321 (2013.01); C12N 2310/3233 (2013.01); C12N 2320/33 (2013.01);
Abstract

The invention relates to a method where a molecule is used for inducing and/or promoting the skipping of at least one of the exons 51-53, 55, 57 and 59 of the DMD pre-mRNA in a patient, preferably in an isolated cell of a patient. The method comprising providing the cell and/or the patient with a molecule. The invention also relates to the molecule and its composition that is being used for inducing exon skipping.

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van Deutekom, Judith Christina Theodora. (2016). Methods and means for efficient skipping of at least one of the exons 51-53, 55, 57 and 59 of the human duchenne muscular dystrophy gene (U.S. Patent No. 9499818). U.S. Patent and Trademark Office. https://idiyas.com/patent/badge/9499818

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