The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Jun. 02, 2015
Filed:
Jul. 19, 2011
Wei Zheng, Potomac, MD (US);
Juan Jose Marugan, Gaithersburg, MD (US);
KE Liu, Cambridge, MD (US);
Noel Terrence Southall, Chevy Chase, MD (US);
Christopher P Austin, Potomac, MD (US);
Wei Zheng, Potomac, MD (US);
Juan Jose Marugan, Gaithersburg, MD (US);
Ke Liu, Cambridge, MD (US);
Noel Terrence Southall, Chevy Chase, MD (US);
Christopher P Austin, Potomac, MD (US);
Abstract
This disclosure relates generally to the treatment of lysosomal storage disorders. Specifically, the disclosure relates to a novel use of delta tocopherol in the treatment of diseases and conditions related to lysosomal storage disorders. Included in the present disclosure is a method for the modulation of cholesterol recycling. Further, the disclosure relates to conditions such as Niemann-Pick type C disease, Farber disease, Niemann-Pick type A disease, Wolman disease and Tay Sachs disease. Further included in the present disclosure is a method for treating lysosomal storage disorders comprising the administration of delta tocopherol. Further included in the present disclosure is a method for treating lysosomal storage disorders comprising the administration of delta tocopherol in combination with cyclodextrin to a patient in need thereof.