The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Oct. 21, 2025
Filed:
Oct. 04, 2019
Applicant:
University of Massachusetts, Boston, MA (US);
Inventor:
Miguel Sena Esteves, Westford, MA (US);
Assignee:
University of Massachusetts, Boston, MA (US);
Attorney:
Primary Examiner:
Int. Cl.
CPC ...
C12N 15/86 (2006.01); A61K 48/00 (2006.01); A61P 3/00 (2006.01); C12N 9/24 (2006.01);
U.S. Cl.
CPC ...
C12N 15/86 (2013.01); A61P 3/00 (2018.01); C12N 9/2402 (2013.01); C12Y 302/01052 (2013.01); A61K 48/00 (2013.01); C12N 2750/14143 (2013.01); C12N 2830/42 (2013.01);
Abstract
Aspects of the disclosure relate to compositions and methods for the treatment of lysosomal storage disorders, such as GM1 gangliosidosis, Tay Sachs disease, and Sandhoff disease. In some embodiments, the compositions comprise viral vectors encoding beta-galactosidase. In some embodiments, the compositions comprise viral vectors encoding beta-hexosaminidase subunits (e.g. HEXA, HEXB, or combinations thereof).
Esteves, Miguel. (2025). Raav vectors for the treatment of gm1 and gm2 gangliosidosis (U.S. Patent No. 12448629). U.S. Patent and Trademark Office. https://idiyas.com/patent/badge/12448629
Data source: USPTO (United States Patent and Trademark Office) public patent records. Weekly synchronization. How IDiyas builds this profile