The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Apr. 29, 2025
Filed:
Oct. 14, 2022
Applicant:
Research Institute AT Nationwide Children's Hospital, Columbus, OH (US);
Inventors:
Louise Rodino-Klapac, Columbus, OH (US);
Jerry R. Mendell, Columbus, OH (US);
Assignee:
Research Institute at Nationwide Children's Hospital, Columbus, OH (US);
Attorney:
Primary Examiner:
Assistant Examiner:
Int. Cl.
CPC ...
A61K 48/00 (2005.12); A61K 38/17 (2005.12); A61P 21/00 (2005.12); C12N 15/86 (2005.12);
U.S. Cl.
CPC ...
A61K 48/0066 (2012.12); A61K 38/1719 (2012.12); A61P 21/00 (2017.12); C12N 15/86 (2012.12); C12N 2750/14143 (2012.12); C12N 2750/14145 (2012.12); C12N 2830/15 (2012.12);
Abstract
Described herein are methods of treating muscular dystrophy comprising administering a self complementary recombinant AAV (rAAV) ScAAVrh74.MIHCK7.h8GCB vector, methods of expressing beta-sarcoglycan gene in a patient, pharmaceutical compositions comprising the rAAV, and methods of generating the rAAV.