The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Jan. 21, 2025
Filed:
Sep. 25, 2020
Applicant:
The United States of America, As Represented BY the Secretary, Department of Health and Human Services, Bethesda, MD (US);
Inventors:
Charles P. Venditti, Kensington, MD (US);
Randy Chandler, Washington, DC (US);
William J. Pavan, Derwood, MD (US);
Assignee:
Attorney:
Primary Examiner:
Int. Cl.
CPC ...
A61K 35/761 (2015.01); A61K 48/00 (2006.01); A61P 3/00 (2006.01); A61P 25/28 (2006.01); C07K 14/075 (2006.01); C12N 7/04 (2006.01); C12N 15/86 (2006.01); C12N 15/861 (2006.01);
U.S. Cl.
CPC ...
A61K 35/761 (2013.01); A61K 48/005 (2013.01); A61P 3/00 (2018.01); A61P 25/28 (2018.01); C07K 14/075 (2013.01); C12N 7/04 (2013.01); C12N 15/86 (2013.01); C12N 15/8616 (2013.01); C12N 2710/10022 (2013.01); C12N 2710/10034 (2013.01); C12N 2710/10045 (2013.01); C12N 2750/14143 (2013.01);
Abstract
Provided herein are compositions and methods for the viral gene therapy (e.g., AAV-directed gene therapy) of cholesterol storage diseases or disorders, such as Niemann-Pick disease, Type C.