The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Oct. 15, 2024
Filed:
Jun. 20, 2018
Applicant:
The United State of America, As Represented BY the Secretary, Department of Health and Human Services, Bethesda, MD (US);
Inventors:
Charles P. Venditti, Potomac, MD (US);
William J. Pavan, Derwood, MD (US);
Randy J. Chandler, Chevy Chase, MD (US);
Assignee:
Attorney:
Primary Examiner:
Int. Cl.
CPC ...
C12N 15/67 (2006.01); C12N 15/52 (2006.01); C12N 15/62 (2006.01); C12N 15/86 (2006.01);
U.S. Cl.
CPC ...
C12N 15/67 (2013.01); C12N 15/52 (2013.01); C12N 15/62 (2013.01); C12N 15/86 (2013.01); C07K 2319/10 (2013.01); C12N 2710/10243 (2013.01); C12N 2799/022 (2013.01);
Abstract
The present disclosure provides compositions for viral gene therapy, e.g. Adeno-Associated virus-directed gene therapy, and methods of using the same for the treatment and/or prevention of cholesterol storage diseases or disorders, such as Niemann-Pick disease, Type C.