The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
Jul. 16, 2024

Filed:

Apr. 04, 2019
Applicants:

Genethon, Evry, FR;

Institut National DE LA Sante ET DE LA Recherche Medicale, Paris, FR;

Universite D'evry Val D'essonne, Evry, FR;

Sorbonne Universite, Paris, FR;

Association Institut DE Myologie, Paris, FR;

Inventors:

Isabelle Richard, Corbeil, FR;

Evelyne Gicquel, Vert-le-Petit, FR;

Federico Mingozzi, Paris, FR;

Attorney:
Primary Examiner:
Assistant Examiner:
Int. Cl.
CPC ...
C07K 14/005 (2006.01); A61K 48/00 (2006.01); A61P 25/28 (2006.01); C07K 14/075 (2006.01); C12N 7/00 (2006.01); C12N 9/22 (2006.01); C12N 15/11 (2006.01); C12N 15/86 (2006.01);
U.S. Cl.
CPC ...
C07K 14/005 (2013.01); A61P 25/28 (2018.01); C07K 14/075 (2013.01); C12N 7/00 (2013.01); C12N 9/22 (2013.01); C12N 15/111 (2013.01); C12N 15/86 (2013.01); A61K 48/00 (2013.01); C12N 2310/20 (2017.05); C12N 2750/14121 (2013.01); C12N 2750/14122 (2013.01); C12N 2750/14143 (2013.01); C12N 2750/14152 (2013.01); C12N 2750/14171 (2013.01);
Abstract

The invention relates to a recombinant adeno-associated virus (AAV) capsid protein, which is a hybrid between AAV serotype 9 (AAV9) and AAV serotype 74 (AAVrh74) capsid proteins, wherein said recombinant hybrid AAV capsid protein has a reduced liver tropism compared to the parent AAV9 and AAVrh74 capsid proteins. The invention relates also to the derived hybrid AAV serotype vector particles packaging a gene of interest and their use in gene therapy, in particular for treating neuromuscular genetic diseases.


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