The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
Apr. 02, 2024

Filed:

Mar. 29, 2020
Applicant:

The Scripps Research Institute, La Jolla, CA (US);

Inventors:

Jeffery W. Kelly, La Jolla, CA (US);

Gareth John Morgan, La Jolla, CA (US);

Nicholas Lok Yan, La Jolla, CA (US);

Hank Michael James Petrassi, La Jolla, CA (US);

Assignee:
Attorneys:
Primary Examiner:
Int. Cl.
CPC ...
C07D 471/10 (2006.01); C07C 255/30 (2006.01); C07C 311/39 (2006.01); C07C 317/24 (2006.01); C07D 207/06 (2006.01); C07D 207/48 (2006.01); C07D 215/227 (2006.01); C07D 233/72 (2006.01); C07D 235/02 (2006.01); C07D 239/47 (2006.01); C07D 311/18 (2006.01); C07D 319/06 (2006.01); C07D 405/04 (2006.01); C07D 405/06 (2006.01); C07D 405/12 (2006.01); C07D 407/12 (2006.01); C07D 487/10 (2006.01);
U.S. Cl.
CPC ...
C07D 405/12 (2013.01); C07C 255/30 (2013.01); C07C 311/39 (2013.01); C07C 317/24 (2013.01); C07D 207/06 (2013.01); C07D 207/48 (2013.01); C07D 215/227 (2013.01); C07D 233/72 (2013.01); C07D 235/02 (2013.01); C07D 239/47 (2013.01); C07D 311/18 (2013.01); C07D 319/06 (2013.01); C07D 405/04 (2013.01); C07D 405/06 (2013.01); C07D 407/12 (2013.01); C07D 471/10 (2013.01); C07D 487/10 (2013.01);
Abstract

In immunoglobulin light chain amyloidosis (AL), the unique antibody light chain (LC) protein that is secreted by monoclonal plasma cells in each patient misfolds and/or aggregates, a process leading to organ degeneration. For treating AL patients, such as those with substantial cardiac involvement who have difficulty tolerating existing chemotherapy regimens, provided herein are small molecule compounds of Formula Ia, Formula Ib, and Formula II that are kinetic stabilizers of the native dimeric structure of full-length LCs, which compounds can slow or stop the amyloidogenicity cascade at its origin.


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