The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
Jan. 02, 2024

Filed:

Aug. 07, 2019
Applicants:

Sangamo Therapeutics, Inc., Richmond, CA (US);

Roselia C. Santana, Walnut Creek, CA (US);

Inventors:

Dale Ando, Richmond, CA (US);

Cheryl Wong Po Foo, Richmond, CA (US);

Sagar A. Vaidya, Richmond, CA (US);

Shelley Q. Wang, Richmond, CA (US);

Assignee:

Sangamo Therapeutics, Inc., Brisbane, CA (US);

Attorney:
Primary Examiner:
Int. Cl.
CPC ...
A61K 48/00 (2006.01); A61P 3/00 (2006.01); G01N 33/66 (2006.01); C12Q 1/34 (2006.01); A61K 38/47 (2006.01);
U.S. Cl.
CPC ...
A61K 48/005 (2013.01); A61K 38/47 (2013.01); A61P 3/00 (2018.01); C12Q 1/34 (2013.01); C12Y 301/06013 (2013.01); C12Y 302/01076 (2013.01); G01N 33/66 (2013.01);
Abstract

Described herein are methods and compositions for treating MPS I (Hurler/Hurler-Scheie/Scheie Syndrome) by administering to the subject a composition comprising a iduronidase (IDUA) polynucleotide. In one aspect, provided is a method of reducing, delaying and/or eliminating one or more of the need for additional treatment procedures, the onset, progression and/or severity of symptoms in a subject with MPS I, by administering to the subject a composition comprising a iduronidase (IDUA) polynucleotide.


Find Patent Forward Citations

Loading…