The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Jul. 18, 2023
Filed:
May. 18, 2020
The General Hospital Corporation, Boston, MA (US);
The United States of America, As Represented BY the Secretary, Department of Health and Human Services, Bethesda, MD (US);
Susan A. Slaugenhaupt, Hingham, MA (US);
Graham Johnson, Sanbornton, NH (US);
William D. Paquette, Amsterdam, NY (US);
Wei Zhang, Sharon, MA (US);
Juan Marugan, Gaithersburg, MD (US);
The General Hospital Corporation, Boston, MA (US);
The United States Of America, as represented by the secretary, Department of Health and Human Services, Bethesda, MD (US);
Abstract
Provided herein are compounds useful for improving mRNA splicing in a cell. Exemplary compounds provided herein are useful for improving mRNA splicing in genes comprising at least one exon ending in the nucleotide sequence CAA. Methods for preparing the compounds and methods of treating diseases of the central nervous system are also provided.