The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Feb. 07, 2023
Filed:
Dec. 19, 2014
Bcn Peptides, S.a., Sant Quinti De Mediona Barcelona, ES;
Josep Farrera-Sinfreu, Tírvia, ES;
Leslie Matalonga Borrel, Barcelona, ES;
Laura Gort Mas, Balenyà, ES;
Roberto Pascual Martínez, Alicante, ES;
Antonio Ferrer Montiel, Alicante, ES;
Antonia Ribes Rubió, Esplugues De Llobregat, ES;
Berta Ponsati Obiols, Barcelona, ES;
BCN PEPTIDES, S.A., Sant Quinti de Mediona, ES;
Abstract
The invention provides a therapy for lysosomal storage diseases and glycogenosis by treatment with compounds that promote exocytosis, preferably lysosomal exocytosis. The treatment of cells from patients affected by different lysosomal storage disorders with exocytosis activating compounds leads to a decrease in the accumulation of toxic substrate in the lysosomes, thus allowing the treatment, prevention and relief of the symptoms of many lysosomal storage disorders.