The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
Jul. 19, 2022

Filed:

Dec. 05, 2016
Applicants:

Sorbonne Universite, Paris, FR;

Inserm (Institut National DE LA Sante ET DE LA Recherche Medicale), Paris, FR;

Centre National DE LA Recherche Scientifique, Paris, FR;

Friedrich Miescher Institute for Biomedical Research, Basel, CH;

Inventors:

Deniz Dalkara, Alfortville, FR;

Serge Picaud, Avon, FR;

Melissa Desrosiers, Alfortville, FR;

Jose-Alain Sahel, Paris, FR;

Jens Duebel, Paris, FR;

Alexis Bemelmans, Chatou, FR;

Botond Roska, Oberwil, CH;

Attorney:
Primary Examiner:
Int. Cl.
CPC ...
C12N 15/113 (2010.01); C12N 15/85 (2006.01); A61P 25/28 (2006.01); A61P 25/02 (2006.01); A61P 27/00 (2006.01); A61K 31/7105 (2006.01); A61K 31/711 (2006.01); A61K 48/00 (2006.01);
U.S. Cl.
CPC ...
C12N 15/113 (2013.01); A61K 31/711 (2013.01); A61K 31/7105 (2013.01); A61K 48/0058 (2013.01); A61P 25/02 (2018.01); A61P 25/28 (2018.01); A61P 27/00 (2018.01); C12N 15/85 (2013.01); C12N 2750/14132 (2013.01); C12N 2750/14143 (2013.01); C12N 2750/14145 (2013.01); C12N 2840/105 (2013.01);
Abstract

The present invention relates to a nucleic acid sequence derived from the regulatory region of the human gamma-synuclein gene and having a promoter activity in retinal ganglion cells. The present invention also relates to expression cassettes or vectors comprising said promoter operably linked to a nucleic acid sequence encoding a polypeptide of interest as well as viral particles or host cells comprising said expression cassette or vector. The present invention also relates to the use of said expression cassettes, vectors, viral particles or cells in the treatment of ocular disease, in particular ocular disease associated with retinal ganglion cell or photoreceptor cell degeneration.


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