The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.

The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.

Date of Patent:
Oct. 05, 2021

Filed:

Aug. 21, 2018
Applicant:

University of Massachusetts, Boston, MA (US);

Inventor:

Tariq M. Rana, San Diego, CA (US);

Assignee:

UNIVERSITY OF MASSACHUSETTS, Boston, MA (US);

Attorneys:
Primary Examiner:
Int. Cl.
CPC ...
C07H 21/04 (2006.01); C12N 15/113 (2010.01); C07D 213/69 (2006.01); C07D 495/04 (2006.01); C12N 15/11 (2006.01); A61K 38/00 (2006.01); A61K 48/00 (2006.01);
U.S. Cl.
CPC ...
C12N 15/113 (2013.01); C07D 213/69 (2013.01); C07D 495/04 (2013.01); C12N 15/111 (2013.01); C12N 15/1137 (2013.01); C12Y 207/11022 (2013.01); A01K 2217/075 (2013.01); A61K 38/00 (2013.01); A61K 48/00 (2013.01); C12N 2310/14 (2013.01); C12N 2310/31 (2013.01); C12N 2310/315 (2013.01); C12N 2310/322 (2013.01); C12N 2310/33 (2013.01); C12N 2310/335 (2013.01); C12N 2310/3341 (2013.01); C12N 2310/3513 (2013.01); C12N 2310/53 (2013.01); C12N 2320/51 (2013.01);
Abstract

The present invention provides compositions for RNA interference and methods of use thereof. In particular, the invention provides small interfering RNAs (siRNAs) having modification that enhance the stability of the siRNA without a concomitant loss in the ability of the siRNA to participate in RNA interference (RNAi). The invention also provides siRNAs having modification that increase targeting efficiency. Modifications include chemical crosslinking between the two complementary strands of an siRNA and chemical modification of a 3' terminus of a strand of an siRNA. Preferred modifications are internal modifications, for example, sugar modification, nucleobase modification and/or backbone modifications. Such modifications are also useful, e.g., to improve uptake of the siRNA by a cell. Functional and genomic and proteomic methods are featured. Therapeutic methods are also featured.


Find Patent Forward Citations

Loading…