The patent badge is an abbreviated version of the USPTO patent document. The patent badge does contain a link to the full patent document.
The patent badge is an abbreviated version of the USPTO patent document. The patent badge covers the following: Patent number, Date patent was issued, Date patent was filed, Title of the patent, Applicant, Inventor, Assignee, Attorney firm, Primary examiner, Assistant examiner, CPCs, and Abstract. The patent badge does contain a link to the full patent document (in Adobe Acrobat format, aka pdf). To download or print any patent click here.
Patent No.:
Date of Patent:
Feb. 02, 2021
Filed:
Aug. 26, 2016
Applicant:
Sarepta Therapeutics, Inc., Cambridge, MA (US);
Inventors:
Marco A. Passini, Cambridge, MA (US);
Gunnar J. Hanson, Cambridge, MA (US);
Assignee:
SAREPTA THERAPEUTICS, INC., Cambridge, MA (US);
Primary Examiner:
Int. Cl.
CPC ...
A61K 31/712 (2006.01); C12N 15/11 (2006.01); A61K 31/7125 (2006.01); A61P 25/14 (2006.01); A61P 21/00 (2006.01);
U.S. Cl.
CPC ...
A61K 31/712 (2013.01); A61K 31/7125 (2013.01); A61P 21/00 (2018.01); A61P 25/14 (2018.01); C12N 15/11 (2013.01); C12N 2310/3145 (2013.01); C12N 2310/3233 (2013.01); C12N 2310/33 (2013.01);
Abstract
The present disclosure relates to modified antisense oligomers and related compositions and methods for increasing the expression of functional SMN protein and methods for treating spinal muscular atrophy and relates to inducing inclusion of exon 7 in SMN2 mRNA.